Incident cancers and late mortality in Australian children treated by allogeneic stem cell transplantation for non-malignant diseases

Pediatr Blood Cancer. 2017 Jan;64(1):197-202. doi: 10.1002/pbc.26219. Epub 2016 Sep 26.

Abstract

Background: Hematopoietic stem cell transplantation (HSCT) is a life-saving procedure for children with a variety of non-malignant conditions. However, these children face an increased risk of late death and incident cancers after HSCT, which may occur many years after their initial HSCT.

Procedure: We examined cancer occurrence and late mortality in a population-based cohort of 318 Australian children who underwent allogeneic HSCT for non-malignant disease. Standardized incident ratios (SIRs) and standardized mortality ratios (SMRs) were calculated and compared with population controls.

Results: We identified six (1.9%) cancers at a median 9.2 years post-HSCT. Cancer occurred 15 times more frequently than in the general population (SIR 15.4, 95% CI = 6.9-34.2). Of the 198 patients who survived for at least 2 years post-HSCT, 11 (5.6%) died at a median 7.5 years post-HSCT. The mortality rate was 17 times higher than in the general population (SMR 17.5, 95% CI = 9.7-31.2).

Discussion: Children transplanted for non-malignant conditions require evidence-based survivorship programs to reduce excess morbidity and mortality.

Keywords: allogeneic stem cell transplantation; cancer incidence; children; late mortality; non-malignant; risk.

MeSH terms

  • Adolescent
  • Anemia, Aplastic / complications
  • Anemia, Aplastic / therapy*
  • Australia / epidemiology
  • Bone Marrow Diseases / complications
  • Bone Marrow Diseases / therapy*
  • Bone Marrow Failure Disorders
  • Child
  • Child, Preschool
  • Female
  • Follow-Up Studies
  • Graft vs Host Disease / epidemiology
  • Graft vs Host Disease / etiology
  • Graft vs Host Disease / mortality*
  • Hematopoietic Stem Cell Transplantation / adverse effects*
  • Hemoglobinuria, Paroxysmal / complications
  • Hemoglobinuria, Paroxysmal / therapy*
  • Humans
  • Incidence
  • Infant
  • Infant, Newborn
  • Male
  • Metabolism, Inborn Errors / complications
  • Metabolism, Inborn Errors / therapy*
  • Neoplasms / epidemiology
  • Neoplasms / etiology
  • Neoplasms / mortality*
  • Prognosis
  • Risk Factors
  • Survival Rate
  • Transplantation, Homologous
  • X-Linked Combined Immunodeficiency Diseases / complications
  • X-Linked Combined Immunodeficiency Diseases / therapy*