Ten Years of the International Pompe Survey: Patient-Reported Outcomes as a Reliable Tool for Studying Treated and Untreated Children and Adults with Non-Classic Pompe Disease
J Neuromuscul Dis
.
2015;2(s1):S35.
Authors
J C van der Meijden
1
,
D Güngör
1
,
M E Kruijshaar
1
,
A D J Muir
2
,
H A Broekgaarden
3
,
A T van der Ploeg
1
Affiliations
1
Center for Lysosomal and Metabolic diseases, Erasmus MC University Medical Center, Rotterdam, Netherlands.
2
International Pompe Association, Association for Glycogen Storage Disease UK, UK.
3
International Pompe Association, Vereniging Spierziekten Nederland, Netherlands.
PMID:
27858630
No abstract available