Enhancing the Cell Permeability and Metabolic Stability of Peptidyl Drugs by Reversible Bicyclization

Angew Chem Int Ed Engl. 2017 Feb 1;56(6):1525-1529. doi: 10.1002/anie.201610888. Epub 2016 Dec 30.

Abstract

Therapeutic applications of peptides are currently limited by their proteolytic instability and impermeability to the cell membrane. A general, reversible bicyclization strategy is now reported to increase both the proteolytic stability and cell permeability of peptidyl drugs. A peptide drug is fused with a short cell-penetrating motif and converted into a conformationally constrained bicyclic structure through the formation of a pair of disulfide bonds. The resulting bicyclic peptide has greatly enhanced proteolytic stability as well as cell-permeability. Once inside the cell, the disulfide bonds are reduced to produce a linear, biologically active peptide. This strategy was applied to generate a cell-permeable bicyclic peptidyl inhibitor against the NEMO-IKK interaction.

Keywords: bicyclization; cell-penetrating peptides; cyclic peptides; nemo inhibitors; protein-protein interactions.

Publication types

  • Research Support, N.I.H., Extramural

MeSH terms

  • Amino Acid Sequence
  • Cell Membrane Permeability
  • Cell-Penetrating Peptides / chemistry*
  • Cell-Penetrating Peptides / metabolism
  • Cell-Penetrating Peptides / pharmacokinetics
  • Cell-Penetrating Peptides / pharmacology*
  • Drug Discovery
  • Drug Stability
  • HeLa Cells
  • Humans
  • I-kappa B Kinase / metabolism
  • Peptides, Cyclic / chemistry*
  • Peptides, Cyclic / metabolism
  • Peptides, Cyclic / pharmacokinetics
  • Peptides, Cyclic / pharmacology*
  • Pharmacokinetics
  • Protein Interaction Maps / drug effects*
  • Proteolysis
  • Solid-Phase Synthesis Techniques

Substances

  • Cell-Penetrating Peptides
  • IKBKG protein, human
  • Peptides, Cyclic
  • I-kappa B Kinase