Prognostic Significance of Residual Acute Myeloid Leukemia in Bone Marrow Samples Taken Prior to Allogeneic Hematopoietic Cell Transplantation

Am J Clin Pathol. 2017 Jan 1;147(1):50-59. doi: 10.1093/ajcp/aqw203.

Abstract

Objectives: We sought to identify features in routine evaluation of pre-hematopoietic cell transplantation (HCT) bone marrow samples from patients with acute myeloid leukemia (AML) that influenced patient outcome.

Methods: Of 140 patients, evidence of residual leukemia (RL) was identified in 38 (27%) of pre-HCT samples, as defined by 5% or more aspirate blasts, increased blood blasts, clustered or necrotic blasts on biopsy specimens, and/or leukemia-associated karyotypic abnormalities.

Results: Morphologic or karyotypic evidence of RL was significantly associated with shorter leukemia-free survival (LFS) compared with cases without identifiable RL (median, 7.1 vs 28.3 months; P < .0001). Upon multivariable analysis, RL, prior relapse, age, high-risk karyotype, and alternate donor source were each independently associated with shorter LFS. RL in pre-HCT samples was more strongly associated with shorter LFS in patients with intermediate or favorable-risk AML karyotype ( P = .001) than secondary or adverse karyotype-risk AML ( P = .04).

Conclusions: Rigorous morphologic and karyotypic evaluation of pretransplant marrows is practical and important for posttransplant prognosis.

Keywords: Acute myeloid leukemia; Allogeneic hematopoietic cell transplantation; Bone marrow biopsy; Minimal residual disease.

MeSH terms

  • Adult
  • Aged
  • Bone Marrow / pathology
  • Female
  • Hematopoietic Stem Cell Transplantation / mortality*
  • Humans
  • Kaplan-Meier Estimate
  • Leukemia, Myeloid, Acute / mortality*
  • Leukemia, Myeloid, Acute / pathology*
  • Leukemia, Myeloid, Acute / surgery
  • Male
  • Middle Aged
  • Neoplasm, Residual / pathology
  • Prognosis
  • Proportional Hazards Models
  • Retrospective Studies
  • Transplantation, Homologous
  • Young Adult