Concomitant Use of Panobinostat and Reirradiation in Progressive DIPG: Report of 2 Cases

J Pediatr Hematol Oncol. 2017 Aug;39(6):e332-e335. doi: 10.1097/MPH.0000000000000806.

Abstract

Diffuse intrinsic pontine glioma (DIPG) remains a devastating disease. Panobinostat has been shown to have therapeutic efficacy both in vitro and in DIPG orthotopic xenograft models; however, clinical data in patients with DIPG are lacking. We present 2 cases of DIPG, who were treated with panobinostat at 22 to 25 mg/m/dose, 3 times weekly for 2 weeks in 3-week cycles and concomitant reirradiation after disease progression. Two episodes of asymptomatic thrombocytopenia were observed in 1 patient. Hyperacetylation of histone H4 of peripheral blood mononuclear cells was evident following treatment. In our experience, panobinostat administered with reirradiation was well tolerated at a relatively higher dose than that used in adult studies.

Publication types

  • Case Reports

MeSH terms

  • Acetylation
  • Child, Preschool
  • Combined Modality Therapy
  • Disease Progression
  • Drug Administration Schedule
  • Female
  • Glioma / drug therapy*
  • Glioma / radiotherapy*
  • Histones / metabolism
  • Humans
  • Hydroxamic Acids / administration & dosage*
  • Indoles / administration & dosage*
  • Panobinostat
  • Re-Irradiation
  • Thrombocytopenia / etiology
  • Treatment Outcome

Substances

  • Histones
  • Hydroxamic Acids
  • Indoles
  • Panobinostat