PCSK9 inhibitor access barriers-issues and recommendations: Improving the access process for patients, clinicians and payers

Clin Cardiol. 2017 Apr;40(4):243-254. doi: 10.1002/clc.22713. Epub 2017 Mar 22.

Abstract

The proprotein convertase subtilisin/kexin type 9 inhibitors or monoclonal antibodies likely represent the greatest advance in lipid management in 30 years. In 2015 the US Food and Drug Administration approved both alirocumab and evolocumab for high-risk patients with familial hypercholesterolemia (FH) and clinical atherosclerotic cardiovascular disease requiring additional lowering of low-density lipoprotein cholesterol. Though many lipid specialists, cardiovascular disease prevention experts, endocrinologists, and others prescribed the drugs on label, they found their directives denied 80% to 90% of the time. The high frequency of denials prompted the American Society for Preventive Cardiology (ASPC), to gather multiple stakeholder organizations including the American College of Cardiology, National Lipid Association, American Association of Clinical Endocrinologists (AACE), and FH Foundation for 2 town hall meetings to identify access issues and implement viable solutions. This article reviews findings recognized and solutions suggested by experts during these discussions. The article is a product of the ASPC, along with each author writing as an individual and endorsed by the AACE.

Keywords: Coronary Artery Disease; Familial Hypercholesterolemia; Hepatocyte; Low-Density Lipoprotein Cholesterol; Pharmacy Benefits Manager; Proprotein Convertase Subtilisin/Kexin Type 9.

Publication types

  • Review

MeSH terms

  • Antibodies, Monoclonal / economics
  • Antibodies, Monoclonal / therapeutic use*
  • Antibodies, Monoclonal, Humanized
  • Cost-Benefit Analysis
  • Drug Costs*
  • Humans
  • Hypercholesterolemia* / blood
  • Hypercholesterolemia* / drug therapy
  • Hypercholesterolemia* / economics
  • Indole Alkaloids / economics
  • Indole Alkaloids / therapeutic use*
  • PCSK9 Inhibitors*
  • Practice Guidelines as Topic*
  • Proprotein Convertase 9 / blood

Substances

  • Antibodies, Monoclonal
  • Antibodies, Monoclonal, Humanized
  • Indole Alkaloids
  • PCSK9 Inhibitors
  • evodamine
  • PCSK9 protein, human
  • Proprotein Convertase 9
  • alirocumab