Heterozygous Nonsense Mutation in the Androgen Receptor Gene Associated with Partial Androgen Insensitivity Syndrome in an Individual with 47,XXY Karyotype

Sex Dev. 2017;11(2):78-81. doi: 10.1159/000468957. Epub 2017 Apr 29.

Abstract

There are only 2 patients with 47,XXY karyotype and androgen receptor (AR) gene mutation reported in the literature, and both are diagnosed as complete androgen insensitivity syndrome (CAIS). We report a 22-year-old female with 47,XXY karyotype and atypical external genitalia. Sequencing of AR revealed the heterozygous p.Asn849Lys*32 mutation, and extensive X chromosome microsatellite analysis showed homozygosity for Xp and heterozygosity for Xq, suggesting partial X maternal isodisomy. Partial androgen insensitivity syndrome (PAIS) developed in this case, probably because of the presence of the heterozygous AR mutation and random X- inactivation of the healthy allele. This is the first report of a female patient with 47,XXY karyotype and PAIS phenotype.

Keywords: Androgen insensitivity syndrome; Androgen receptor gene; Heterozygous mutation; Klinefelter syndrome; Somatic mosaicism.

Publication types

  • Case Reports
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Androgen-Insensitivity Syndrome / genetics*
  • Base Sequence
  • Codon, Nonsense / genetics*
  • Exons / genetics
  • Female
  • Genetic Predisposition to Disease*
  • Heterozygote
  • Homozygote
  • Humans
  • Karyotype*
  • Male
  • Microsatellite Repeats / genetics
  • Mutation / genetics*
  • Receptors, Androgen / genetics*
  • Young Adult

Substances

  • AR protein, human
  • Codon, Nonsense
  • Receptors, Androgen