Design, synthesis, and biological evaluation of deuterated phenylpropionic acid derivatives as potent and long-acting free fatty acid receptor 1 agonists

Bioorg Chem. 2018 Feb:76:303-313. doi: 10.1016/j.bioorg.2017.12.012. Epub 2017 Dec 5.

Abstract

The free fatty acid receptor 1 (FFA1) is a potential target due to its function in enhancement of glucose-stimulated insulin secretion. Takeda's compound 1 has robustly in vitro activity for FFA1, but it has been suffered from poor pharmacokinetic (PK) profiles because the phenylpropanoic acid is vulnerable to β-oxidation. To identify orally available agonists, we tried to interdict the metabolically labile group by incorporating two deuterium atoms at the α-position of phenylpropionic acid. Interestingly, the differences of physicochemical properties between hydrogen and deuterium are quite small, but there are many differences in the structure-activity relationship between phenylpropionic acid series and present deuterated series. Further optimizations of deuterated series led to the discovery of compound 18, which exhibited a superior balance in terms of in vitro activity, lipophilicity, and solubility. Better still, compound 18 revealed a lower clearance (CL = 0.44 L/h/kg), higher maximum concentration (Cmax = 7584.27 μg/L), and longer half-life (T1/2 = 4.16 h), resulting in a >23-fold exposure than compound 1. In subsequent in vivo pharmacodynamic studies, compound 18 showed a robustly glucose-lowering effect in rodent without the risk of hypoglycemia.

Keywords: Deuteration; Diabetes; Free fatty acid receptor; Hypoglycemia; Pharmacokinetic profiles.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Animals
  • Deuterium / chemistry*
  • Drug Design*
  • Hypoglycemic Agents / chemical synthesis
  • Hypoglycemic Agents / chemistry
  • Hypoglycemic Agents / pharmacokinetics
  • Hypoglycemic Agents / pharmacology
  • Mice, Inbred ICR
  • Molecular Docking Simulation
  • Molecular Structure
  • Phenylpropionates / chemical synthesis
  • Phenylpropionates / chemistry
  • Phenylpropionates / pharmacokinetics
  • Phenylpropionates / pharmacology*
  • Rats, Sprague-Dawley
  • Receptors, G-Protein-Coupled / agonists*
  • Structure-Activity Relationship

Substances

  • Ffar1 protein, mouse
  • G-protein-coupled receptor 40, rat
  • Hypoglycemic Agents
  • Phenylpropionates
  • Receptors, G-Protein-Coupled
  • Deuterium