Postmortem Genetic Testing for Cardiac Ion Channelopathies in Stillbirths

Circ Genom Precis Med. 2018 Jan;11(1):e001817. doi: 10.1161/CIRCGEN.117.001817. Epub 2018 Jan 11.

Abstract

Background: Although stillbirth is a significant health problem worldwide, the definitive cause of death remains elusive in many cases, despite detailed autopsy. In this study of partly explained and unexplained stillbirths, we used next-generation sequencing to examine an extended panel of 35 candidate genes known to be associated with ion channel disorders and sudden cardiac death.

Methods and results: We examined tissue from 242 stillbirths (≥22 weeks), including those where no definite cause of death could be confirmed after a full autopsy. We obtained high-quality DNA from 70 cases, which were then sequenced for a custom panel of 35 genes, 12 for inherited long- and short-QT syndrome genes (LQT1-LQT12 and SQT1-3), and 23 additional candidate genes derived from genome-wide association studies. We examined the functional significance of a selected variant by patch-clamp electrophysiological recording. No predicted damaging variants were identified in KCNQ1 (LQT1) or KCNH2 (LQT2). A rare putative pathogenic variant was found in KCNJ2(LQT7) in 1 case, and several novel variants of uncertain significance were observed. The KCNJ2 variant (p. R40Q), when assessed by whole-cell patch clamp, affected the function of the channel. There was no significant evidence of enrichment of rare predicted damaging variants within any of the candidate genes.

Conclusions: Although a causative link is unclear, 1 putative pathogenic and variants of uncertain significance variant resulting in cardiac channelopathies was identified in some cases of otherwise unexplained stillbirth, and these variants may have a role in fetal demise.

Clinical trial registration: URL: https://www.clinicaltrials.gov. Unique identifier: NCT01120886.

Keywords: autopsy; cause of death; fetal heart; mutation; stillbirth.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Channelopathies / genetics
  • Channelopathies / pathology*
  • DNA / chemistry
  • DNA / isolation & purification
  • DNA / metabolism
  • ERG1 Potassium Channel / genetics
  • Female
  • Gestational Age
  • Humans
  • KCNQ1 Potassium Channel / genetics
  • Male
  • Polymorphism, Single Nucleotide
  • Potassium Channels, Inwardly Rectifying / genetics
  • Pregnancy
  • Sequence Analysis, DNA
  • Stillbirth / ethnology
  • Stillbirth / genetics*

Substances

  • ERG1 Potassium Channel
  • KCNH2 protein, human
  • KCNJ2 protein, human
  • KCNQ1 Potassium Channel
  • KCNQ1 protein, human
  • Potassium Channels, Inwardly Rectifying
  • DNA

Associated data

  • ClinicalTrials.gov/NCT01120886