[Genetic screening and prenatal diagnosis for high risk families of Fragile X syndrome]

Zhonghua Yi Xue Yi Chuan Xue Za Zhi. 2018 Oct 10;35(5):653-656. doi: 10.3760/cma.j.issn.1003-9406.2018.05.007.
[Article in Chinese]

Abstract

Objective: To assess the value of genetic testing for Fragile X syndrome (FXS).

Methods: A domestically made diagnostic kit based Tri-primer-PCR method was used to detect mutations of the FMR1 gene among 6 pedigrees with unexplained intellectual disability. The results were verified by methylation PCR and Southern blotting.

Results: Pedigrees 1 and 6 were positive for the screening. In pedigree 1, a full-mutation allele with methylation was identified in the proband and his mother, which was passed on to the fetus. In pedigree 6, the proband was mosaic for a full-mutation allele and a pre-mutation allele. His sister was asymptomatic with a full-mutation. His mother carried pre-mutation allele, while his father and sister's baby were normal. The number of CGG repeats of the pedigrees 2 to 5 were in the normal range.

Conclusion: Genetic testing can provide an effective way to prevent FXS caused by FMR1 mutations and enable prenatal diagnosis for families with a high risk for the disease.

MeSH terms

  • Adult
  • Alleles
  • Female
  • Fetal Diseases / diagnosis*
  • Fetal Diseases / genetics
  • Fragile X Mental Retardation Protein
  • Fragile X Syndrome / complications
  • Fragile X Syndrome / embryology*
  • Fragile X Syndrome / genetics*
  • Fragile X Syndrome / psychology
  • Genetic Testing
  • Humans
  • Intellectual Disability / etiology
  • Male
  • Mutation
  • Pedigree
  • Pregnancy
  • Prenatal Diagnosis
  • Young Adult

Substances

  • FMR1 protein, human
  • Fragile X Mental Retardation Protein