Bevacizumab for Hearing Preservation in Neurofibromatosis Type 2: Emphasis on Patient-Reported Outcomes and Toxicities

Otolaryngol Head Neck Surg. 2019 Mar;160(3):526-532. doi: 10.1177/0194599818809085. Epub 2018 Oct 30.

Abstract

Objective: Bevacizumab for hearing preservation in patients with neurofibromatosis type 2 (NF2) is an emerging practice. We set out to characterize the effectiveness and toxicity of bevacizumab in our patient group.

Study design: Case series with chart review.

Setting: Tertiary referral center.

Subjects and methods: Seventeen consecutive patients with NF2 received bevacizumab treatment for vestibular schwannomas, including 2 patients treated to maintain cochlear implant performance. Volumetric analysis of serial magnetic resonance imaging scans was used to evaluate radiographic response, and hearing response was evaluated with serial audiograms. Patient-reported outcomes were also assessed, including subjective hearing improvement, changes in tinnitus, vertigo, headaches, ear pain, and improvement in ability to communicate via telephone.

Results: A positive radiographic response occurred in 8 of 17 (47%) patients and the median tumor volume change was a tumor decrease of 19%. A positive hearing response was recorded in 5 of 9 (56%) patients. Two patients had a word recognition score improvement over 40%. There was an approximately 40% improvement in patient-reported outcomes. Primary toxicities included hypertension, proteinuria, dysgeusia, and amenorrhea.

Conclusion: Bevacizumab treatment was followed by hearing improvement in 56% of patients, while decreased tumor volume was noted in 47%. These outcomes agree favorably with prior reported series. There were significant improvements in patient-reported outcomes that have not been described previously.

Keywords: NF2; bevacizumab; neurofibromatosis type 2; patient-reported outcomes; vestibular schwannoma.

MeSH terms

  • Adolescent
  • Adult
  • Angiogenesis Inhibitors / therapeutic use*
  • Bevacizumab / therapeutic use*
  • Cohort Studies
  • Female
  • Hearing Loss / etiology
  • Hearing Loss / prevention & control*
  • Humans
  • Male
  • Middle Aged
  • Neurofibromatosis 2 / complications*
  • Neurofibromatosis 2 / pathology
  • Neurofibromatosis 2 / therapy
  • Neuroma, Acoustic / complications*
  • Neuroma, Acoustic / pathology
  • Neuroma, Acoustic / therapy
  • Patient Reported Outcome Measures
  • Treatment Outcome
  • Tumor Burden
  • Young Adult

Substances

  • Angiogenesis Inhibitors
  • Bevacizumab