[Cavernoma complicated with biliopatia secondary to type 1 Gaucher disease: report of a Peruvian case]

Rev Gastroenterol Peru. 2018 Jul-Sep;38(3):280-284.
[Article in Spanish]

Abstract

Gaucher disease is an autosomal recessive lysosomal storage disorder characterized by deficiency of beta-glucosidase that would lead to the accumulation of glucosylceramide mainly in cells of the mononuclear phagocytic system causing systemic effectations. We present a patient of twenty years who is suffering from chronic pain in the left hypochondrium with episodes of bleeding for 3 years and sensation of thermal rise, physical examination revealed jaundice and massive splenomegaly, without neurological involvement. Severe osteoporosis, pancytopenia, and the presence of portal vein thrombosis with cavernomatous transformation complicated by portal biliopathy simulating a klatskin tumor, marrow and enzymatic studies were compatible with Gaucher disease, were shown as unexpected findings. he received treatment with imiglucerase, following up. It is a rare case, of great interest, heterogeneity in its clinical manifestations and unpublished by its complication, constituting a challenge to reach its diagnosis of this orphan disease.

Publication types

  • Case Reports

MeSH terms

  • Bile Duct Diseases / etiology*
  • Bile Ducts, Intrahepatic / diagnostic imaging
  • Bile Ducts, Intrahepatic / pathology
  • Dilatation, Pathologic / etiology
  • Enzyme Replacement Therapy
  • Gallbladder / blood supply
  • Gastrointestinal Hemorrhage / etiology*
  • Gaucher Disease / complications*
  • Gaucher Disease / diagnosis
  • Gaucher Disease / drug therapy
  • Glucosylceramidase / therapeutic use
  • Hemangioma, Cavernous / complications*
  • Humans
  • Hypertension, Portal / complications*
  • Hypertension, Portal / diagnostic imaging
  • Male
  • Mesenteric Veins / diagnostic imaging
  • Mesenteric Veins / pathology
  • Portal Vein / abnormalities*
  • Portal Vein / diagnostic imaging
  • Portal Vein / pathology*
  • Renal Veins / diagnostic imaging
  • Renal Veins / pathology
  • Splenectomy
  • Splenic Vein / diagnostic imaging
  • Splenic Vein / pathology
  • Tomography, X-Ray Computed
  • Young Adult

Substances

  • Glucosylceramidase
  • imiglucerase

Supplementary concepts

  • Portal Vein, Cavernous Transformation Of