Discovery of Novel Transient Receptor Potential Vanilloid 4 (TRPV4) Agonists as Regulators of Chondrogenic Differentiation: Identification of Quinazolin-4(3 H)-ones and in Vivo Studies on a Surgically Induced Rat Model of Osteoarthritis

J Med Chem. 2019 Feb 14;62(3):1468-1483. doi: 10.1021/acs.jmedchem.8b01615. Epub 2019 Jan 28.

Abstract

Osteoarthritis (OA) is a degenerative disease characterized by joint destruction and loss of cartilage. There are many unmet needs in the treatment of OA and there are few promising candidates for disease-modifying OA drugs, particularly, anabolic agents. Here, we describe the identification of novel quinazolin-4(3 H)-one derivatives, which stimulate chondrocyte cartilage matrix production via TRPV4 and mitigate damaged articular cartilage. We successfully identified the water-soluble, highly potent quinazolin-4(3 H)-one derivative 36 and studied its intra-articular physicochemical profile to use in in vivo surgical OA model studies. Compound 36·HCl provided relief from OA damage in a rat medial meniscal tear (MT) model. Specifically, 36·HCl dose-dependently suppressed cartilage degradation and enhanced the messenger RNA expression of aggrecan and SOX9 in cartilage isolated from MT-operated rat knees compared with knees treated with vehicle. These results suggest that 36 induces anabolic changes in articular cartilage and consequently reduces OA progression.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Aggrecans / genetics
  • Animals
  • Cartilage, Articular / pathology
  • Cell Differentiation / drug effects*
  • Chondrocytes / metabolism*
  • HEK293 Cells
  • Humans
  • Male
  • Menisci, Tibial / pathology
  • Mice
  • Molecular Structure
  • Osteoarthritis / drug therapy*
  • Osteoarthritis / pathology
  • Quinazolinones / chemical synthesis
  • Quinazolinones / chemistry
  • Quinazolinones / therapeutic use*
  • RNA, Messenger / metabolism
  • Rats, Sprague-Dawley
  • SOX9 Transcription Factor / genetics
  • Structure-Activity Relationship
  • TRPV Cation Channels / agonists*

Substances

  • Aggrecans
  • Quinazolinones
  • RNA, Messenger
  • SOX9 Transcription Factor
  • Sox9 protein, rat
  • TRPV Cation Channels
  • Trpv4 protein, rat