Keeping an eye on congenital disorders of O-glycosylation: A systematic literature review

J Inherit Metab Dis. 2019 Jan;42(1):29-48. doi: 10.1002/jimd.12025.

Abstract

Congenital disorders of glycosylation (CDG) are a rapidly growing family comprising >100 genetic diseases. Some 25 CDG are pure O-glycosylation defects. Even among this CDG subgroup, phenotypic diversity is broad, ranging from mild to severe poly-organ/system dysfunction. Ophthalmic manifestations are present in 60% of these CDG. The ophthalmic manifestations in N-glycosylation-deficient patients have been described elsewhere. The present review documents the spectrum and incidence of eye disorders in patients with pure O-glycosylation defects with the aim of assisting diagnosis and management and promoting research.

Publication types

  • Research Support, Non-U.S. Gov't
  • Systematic Review

MeSH terms

  • Animals
  • Congenital Disorders of Glycosylation / diagnosis*
  • Congenital Disorders of Glycosylation / pathology*
  • Eye Diseases / diagnosis*
  • Eye Diseases / pathology*
  • Glycosylation
  • Humans