Cardiac involvement by CMR in different genotypic groups of thalassemia major patients

Blood Cells Mol Dis. 2019 Jul:77:1-7. doi: 10.1016/j.bcmd.2019.01.008. Epub 2019 Mar 7.

Abstract

Beta thalassemia major (β-TM) displays a great deal of phenotypic heterogeneity, not fully investigated in terms of cause-effect. We aimed to detect if different genotypic groups could be related to different levels of cardiac impairment, evaluated by cardiovascular magnetic resonance (CMR). We considered 671 β-TM patients (age 30.1 years, 52.9% females) consecutively enrolled in the Myocardial Iron Overload (MIO) in Thalassemia network. MIO was assessed by T2* technique. Biventricular function was quantified by cine images. Myocardial fibrosis was evaluated by late gadolinium enhancement (LGE) technique. Three groups of patients were identified: heterozygotes β+/β° (N = 279), homozygotes β + (N = 154), homozygotes β° (N = 238). Transfusional needs resulted significantly lower in homozygous β + TM patients when compared to the other groups. The homozygous β + group versus the heterozygous and homozygous β° groups showed higher global heart T2* values (P < 0.0001) and a lower number of patients with a global heart T2* value<20 ms (P < 0.001). The homozygotes β + showed a lower number of patients with a pathological left ventricular ejection fraction (LVEF) than the other two groups (P < 0.05). The β++ TM patients showed less MIO and a concordant better systolic heart function. These data support the knowledge of different genotypic groups in the management of β-TM patients.

Keywords: Beta-thalassemia; Genotype; Iron Overload; Magnetic Resonance Imaging.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Adult
  • Alleles
  • Biomarkers
  • Blood Transfusion
  • Erythrocyte Indices
  • Female
  • Genotype*
  • Heart Diseases / diagnosis*
  • Heart Diseases / etiology*
  • Heart Function Tests
  • Humans
  • Iron Overload / complications
  • Iron Overload / diagnosis
  • Iron Overload / etiology
  • Iron Overload / therapy
  • Magnetic Resonance Imaging* / methods
  • Male
  • Middle Aged
  • Young Adult
  • beta-Globins / genetics*
  • beta-Thalassemia / complications*
  • beta-Thalassemia / diagnosis
  • beta-Thalassemia / genetics*
  • beta-Thalassemia / therapy

Substances

  • Biomarkers
  • beta-Globins