Gene Therapy: Current Applications and Future Possibilities

Adv Pediatr. 2019 Aug:66:37-54. doi: 10.1016/j.yapd.2019.04.001. Epub 2019 May 16.
No abstract available

Keywords: CAR T cell; CRISPR-Cas9; Gene therapy; Human genome editing; Immunotherapy.

Publication types

  • Review

MeSH terms

  • Cystic Fibrosis / diagnosis
  • Cystic Fibrosis / therapy*
  • Female
  • Forecasting
  • Genetic Diseases, Inborn / diagnosis*
  • Genetic Diseases, Inborn / therapy*
  • Genetic Therapy / methods*
  • Genetic Therapy / trends
  • Genomics
  • Humans
  • Male
  • Patient Safety*
  • Risk Assessment
  • Treatment Outcome