No abstract available
Publication types
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Case Reports
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Observational Study
MeSH terms
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Combined Modality Therapy / methods
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Genetic Therapy / methods*
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Humans
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Infant
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Male
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Oligonucleotides / administration & dosage*
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Spinal Muscular Atrophies of Childhood / diagnosis
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Spinal Muscular Atrophies of Childhood / genetics*
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Spinal Muscular Atrophies of Childhood / therapy*
Substances
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Oligonucleotides
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nusinersen