Correction of Bcl-x splicing improves responses to imatinib in chronic myeloid leukaemia cells and mouse models

Br J Haematol. 2020 Jun;189(6):1141-1150. doi: 10.1111/bjh.16472. Epub 2020 Mar 19.

Abstract

Imatinib mesylate (IM) resistance has become a major clinical problem for chronic myeloid leukaemia (CML). It is known that Bcl-x splicing is deregulated and is involved in multiple malignant cancer initiation and chemotherapy resistance, including CML. The aim of the present study was to correct the abnormal splicing of Bcl-x in CML and investigate the subsequent malignant phenotype changes, especially response to IM. The aberrant Bcl-x splicing in CML cells was effectively restored using vivo-Morpholino Antisense Oligomer (vMO). CCK-8 cell viability assay and flow cytometry showed that restoring of Bcl-x splicing increases IM-induced growth inhibition and apoptosis of K562 cells. Moreover, a more significant similar phenomenon was observed in imatinib-resistant CML cell lines K562/G01. Finally, establishment of CML xenograft model had also proved that correcting Bcl-x splicing in vivo can also enhance the anti-tumor effect of IM. Our findings suggest that vMO co-operating with IM can effectively increase the sensitivity of CML cells to IM both in vitro and in vivo, and Bcl-x splicing could become good candidates for chemotherapy-sensitized target in IM-resistant CML.

Keywords: Bcl-x; IMATINIB; chronic myeloid leukaemia; splicing.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Animals
  • Drug Resistance, Neoplasm* / drug effects
  • Drug Resistance, Neoplasm* / genetics
  • Humans
  • Imatinib Mesylate / pharmacology*
  • K562 Cells
  • Leukemia, Myelogenous, Chronic, BCR-ABL Positive* / drug therapy
  • Leukemia, Myelogenous, Chronic, BCR-ABL Positive* / genetics
  • Leukemia, Myelogenous, Chronic, BCR-ABL Positive* / metabolism
  • Leukemia, Myelogenous, Chronic, BCR-ABL Positive* / pathology
  • Mice
  • Mice, Inbred BALB C
  • Mice, Nude
  • Morpholinos / pharmacology*
  • Neoplasms, Experimental* / drug therapy
  • Neoplasms, Experimental* / genetics
  • Neoplasms, Experimental* / metabolism
  • RNA Splicing / drug effects*
  • Xenograft Model Antitumor Assays
  • bcl-X Protein* / biosynthesis
  • bcl-X Protein* / genetics

Substances

  • Morpholinos
  • bcl-X Protein
  • Imatinib Mesylate