Ketamine mouthwash versus placebo in the treatment of severe oral mucositis pain in children with cancer: A randomized double-blind placebo-controlled trial

Pediatr Blood Cancer. 2020 Sep;67(9):e28573. doi: 10.1002/pbc.28573. Epub 2020 Jul 10.

Abstract

Background and aims: Oral mucositis (OM) is a common and distressing toxicity in children on chemotherapy. There are a limited number of safe and effective therapeutic options available for OM. Ketamine oral rinse has shown promising results in a few studies in adults. This randomized, double-blind placebo-controlled trial aimed to test the efficacy of ketamine mouthwash in reducing chemotherapy-induced severe OM pain in children.

Methods: Children aged 8-18 years with severe OM were randomized to a single dose of ketamine mouthwash (4 mg/mL solution; dose 1 mg/kg) or a placebo. A sample size of 44 patients was determined. Pain score (6-point faces scale) was noted at baseline and 15, 30, 45, 60, 120, 180, and 240 min. The outcome variables were a reduction in pain score, need for rescue medications, and adverse events.

Results: The baseline characteristics were comparable in the two groups. The mean OM pain at 60 min decreased by 1.64 points (CI 1.13-2.14) in the ketamine group and 1.32 points (CI 0.76-1.87) in the placebo group (P = 0.425), with a group difference of 0.32 points. Rescue pain medication (at 60 min) was required in 13.6% in the ketamine group and 18.2% in the placebo group (P = 1.000). No significant adverse events were observed.

Conclusions: Among children on cancer chemotherapy with severe OM, ketamine mouthwash at a dose of 1 mg/kg did not significantly reduce OM pain. It did not decrease the need for rescue pain medications. Further research is warranted to test higher doses of ketamine for a clinically significant effect.

Keywords: chemotherapy; children; ketamine mouthwash; oral mucositis pain.

Publication types

  • Comparative Study
  • Randomized Controlled Trial

MeSH terms

  • Adolescent
  • Analgesics / therapeutic use
  • Antineoplastic Combined Chemotherapy Protocols / adverse effects*
  • Cancer Pain / chemically induced
  • Cancer Pain / drug therapy*
  • Cancer Pain / pathology
  • Child
  • Double-Blind Method
  • Female
  • Follow-Up Studies
  • Humans
  • Ketamine / therapeutic use*
  • Male
  • Mouthwashes / therapeutic use*
  • Neoplasms / drug therapy*
  • Neoplasms / pathology
  • Prognosis
  • Prospective Studies
  • Stomatitis / chemically induced
  • Stomatitis / drug therapy*
  • Stomatitis / pathology
  • Survival Rate

Substances

  • Analgesics
  • Mouthwashes
  • Ketamine