Follicular helper T cell profiles predict response to costimulation blockade in type 1 diabetes

Nat Immunol. 2020 Oct;21(10):1244-1255. doi: 10.1038/s41590-020-0744-z. Epub 2020 Aug 3.

Abstract

Follicular helper T (TFH) cells are implicated in type 1 diabetes (T1D), and their development has been linked to CD28 costimulation. We tested whether TFH cells were decreased by costimulation blockade using the CTLA-4-immunoglobulin (Ig) fusion protein (abatacept) in a mouse model of diabetes and in individuals with new-onset T1D. Unbiased bioinformatics analysis identified that inducible costimulatory molecule (ICOS)+ TFH cells and other ICOS+ populations, including peripheral helper T cells, were highly sensitive to costimulation blockade. We used pretreatment TFH profiles to derive a model that could predict clinical response to abatacept in individuals with T1D. Using two independent approaches, we demonstrated that higher frequencies of ICOS+ TFH cells at baseline were associated with a poor clinical response following abatacept administration. Therefore, TFH analysis may represent a new stratification tool, permitting the identification of individuals most likely to benefit from costimulation blockade.

Publication types

  • Clinical Trial
  • Research Support, N.I.H., Extramural
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Abatacept / pharmacology
  • Abatacept / therapeutic use*
  • Animals
  • Biomarkers, Pharmacological
  • CD28 Antigens / genetics
  • CD28 Antigens / metabolism*
  • Cells, Cultured
  • Computational Biology
  • Diabetes Mellitus, Type 1 / diagnosis
  • Diabetes Mellitus, Type 1 / immunology*
  • Diabetes Mellitus, Type 1 / therapy
  • Disease Models, Animal
  • Germinal Center / immunology*
  • Humans
  • Immune Checkpoint Inhibitors / pharmacology
  • Immune Checkpoint Inhibitors / therapeutic use*
  • Immunotherapy / methods*
  • Inducible T-Cell Co-Stimulator Protein / metabolism
  • Mice
  • Mice, Inbred BALB C
  • Mice, Knockout
  • T-Lymphocytes, Helper-Inducer / immunology*
  • Treatment Outcome

Substances

  • Biomarkers, Pharmacological
  • CD28 Antigens
  • Icos protein, mouse
  • Immune Checkpoint Inhibitors
  • Inducible T-Cell Co-Stimulator Protein
  • Abatacept