Saethre-Chotzen syndrome: long-term outcome of a syndrome-specific management protocol

Dev Med Child Neurol. 2021 Jan;63(1):104-110. doi: 10.1111/dmcn.14670. Epub 2020 Sep 9.

Abstract

Aim: To assess the long-term outcomes of our management protocol for Saethre-Chotzen syndrome, which includes one-stage fronto-orbital advancement.

Method: All patients born with Saethre-Chotzen syndrome between January 1992 and March 2017 were included. Evaluated parameters included occipital frontal head circumference (OFC), fundoscopy, neuroimaging (ventricular size, tonsillar position, and the presence of collaterals/an abnormal transverse sinus), polysomnography, and ophthalmological outcomes. The relationship between papilledema and its associated risk factors was evaluated with Fisher's exact test.

Results: Thirty-two patients (21 females, 11 males) were included. Median (SD) age at first surgery was 9.6 months (3.1mo) for patients who were primarily referred to our center (range: 3.6-13.0mo), the median (SD) age at last follow-up was 13 years (5y 7mo; range: 3-25y). Seven patients had papilledema preoperatively, which recurred in two. Two patients had papilledema solely after first surgery. Second cranial vault expansion was indicated in 20%. Thirteen patients had an OFC deflection, indicating restricted skull growth, one patient had ventriculomegaly, and none developed hydrocephalus. Eleven patients had emissary veins, while the transverse sinus was aberrant unilaterally in 13 (hypoplastic n=10 and absent n=3). Four patients had mild tonsillar descent, one of which was a Chiari type I malformation. Four patients had obstructive sleep apnoea (two mild, one moderate, and one severe). An aberrant transverse sinus was associated with papilledema (p=0.01).

Interpretation: Single one-stage fronto-orbital advancement was sufficient to prevent intracranial hypertension for 80% of our patients with Saethre-Chotzen syndrome. Follow-up should focus on OFC deflection and venous anomalies.

MeSH terms

  • Acrocephalosyndactylia / complications
  • Acrocephalosyndactylia / diagnostic imaging
  • Acrocephalosyndactylia / pathology*
  • Acrocephalosyndactylia / surgery*
  • Adolescent
  • Adult
  • Child
  • Child, Preschool
  • Clinical Protocols
  • Computed Tomography Angiography
  • Female
  • Frontal Bone / surgery*
  • Humans
  • Infant
  • Intracranial Hypertension / etiology
  • Intracranial Hypertension / prevention & control*
  • Longitudinal Studies
  • Magnetic Resonance Imaging
  • Male
  • Neuroimaging
  • Neurosurgical Procedures* / methods
  • Orbit / surgery*
  • Outcome Assessment, Health Care*
  • Tomography, Optical Coherence
  • Young Adult