Therapy development for the mucopolysaccharidoses: Updated consensus recommendations for neuropsychological endpoints

Affiliations

• ¹ Knowledge Institute of the Dutch Association of Medical Specialists, Utrecht, Netherlands; Emma Children's Hospital, Amsterdam UMC, University of Amsterdam, Pediatric Clinical Research Office, Amsterdam, Netherlands.
• ² Comradis, Oxford, UK.
• ³ Department of Neurology, University of Rochester Medical Center, Rochester, NY, USA.
• ⁴ Department of Medical Genetics, Child and Family Research Institute, University of British Columbia, Vancouver, BC, Canada.
• ⁵ Department of Pediatrics, University of Minnesota, Minneapolis, MN, USA.
• ⁶ Department of Pediatrics, University of Pittsburgh School of Medicine, Pittsburgh, PA, USA.
• ⁷ Department of Genetics, UFRGS, and Medical Genetics Service, HPCA, Porto Alegre, Brazil.
• ⁸ UCSF Benioff Children's Hospital Oakland, Oakland, CA, USA.
• ⁹ Doulots LLC, Thompson Station, TN, USA.
• ¹⁰ Clinical Paediatric Psychology, Birmingham Children's Hospital NHS Foundation Trust, Birmingham, UK.
• ¹¹ Department of Pediatrics, University of North Carolina at Chapel Hill, Chapel Hill, NC, USA.
• ¹² Department of Pediatric, University Medical Center Hamburg Eppendorf, Hamburg, Germany.
• ¹³ Paediatric Psychosocial Department, Royal Manchester Children's Hospital, Manchester, UK.
• ¹⁴ Berry Consultants LLC, Austin, TX, USA; Vanderbilt University School of Medicine, Nashville, TN, USA.
• ¹⁵ Division of Metabolic Disorders, Children's Hospital of Orange County, Orange, CA, USA.
• ¹⁶ Department of Pediatrics, University of Pittsburgh School of Medicine, Pittsburgh, PA, USA; Shapiro Neuropsychology Consulting LLC, Portland, OR, USA. Electronic address: [email protected].