Gene therapies targeting the liver

Affiliations

• ¹ NIHR Great Ormond Street Hospital Biomedical Research Centre, University College London, London, UK; MRC Laboratory for Molecular Cell Biology, University College London, London, UK.
• ² NIHR Great Ormond Street Hospital Biomedical Research Centre, University College London, London, UK; Gene Transfer Technology Group, EGA Institute for Women's Health, University College London, London WC1E 6HX, UK; Dubowitz Neuromuscular Centre, Molecular Neurosciences Section, Developmental Neurosciences Programme, UCL Great Ormond Street Institute of Child Health, 30 Guilford Street, London WC1N 1EH, UK.
• ³ NIHR Great Ormond Street Hospital Biomedical Research Centre, University College London, London, UK; MRC Laboratory for Molecular Cell Biology, University College London, London, UK. Electronic address: [email protected].