Combination molecular therapies for spinal muscular atrophy: How much is enough?

Muscle Nerve. 2021 Mar;63(3):279-281. doi: 10.1002/mus.27109. Epub 2020 Nov 23.

Authors

Katherine D Mathews¹, Susan T Iannaccone²

Affiliations

¹ Departments of Pediatrics and Neurology, University of Iowa Carver College of Medicine, Iowa City, Iowa, USA.
² Departments of Pediatrics and Neurology, UT Southwestern Medical Center, Dallas, Texas, USA.

PMID: 33118639
DOI: 10.1002/mus.27109

No abstract available

Publication types

Editorial
Comment

MeSH terms

Humans
Muscular Atrophy, Spinal* / drug therapy
Muscular Atrophy, Spinal* / genetics
Spinal Muscular Atrophies of Childhood*

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