An engineered 4-1BBL fusion protein with "activity on demand"

Proc Natl Acad Sci U S A. 2020 Dec 15;117(50):31780-31788. doi: 10.1073/pnas.2013615117. Epub 2020 Nov 25.

Abstract

Engineered cytokines are gaining importance in cancer therapy, but these products are often limited by toxicity, especially at early time points after intravenous administration. 4-1BB is a member of the tumor necrosis factor receptor superfamily, which has been considered as a target for therapeutic strategies with agonistic antibodies or using its cognate cytokine ligand, 4-1BBL. Here we describe the engineering of an antibody fusion protein, termed F8-4-1BBL, that does not exhibit cytokine activity in solution but regains biological activity on antigen binding. F8-4-1BBL bound specifically to its cognate antigen, the alternatively spliced EDA domain of fibronectin, and selectively localized to tumors in vivo, as evidenced by quantitative biodistribution experiments. The product promoted a potent antitumor activity in various mouse models of cancer without apparent toxicity at the doses used. F8-4-1BBL represents a prototype for antibody-cytokine fusion proteins, which conditionally display "activity on demand" properties at the site of disease on antigen binding and reduce toxicity to normal tissues.

Keywords: 4-1BB; armed antibody; cancer immunotherapy; protein engineering; tumor targeting.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • 4-1BB Ligand / administration & dosage*
  • 4-1BB Ligand / genetics
  • 4-1BB Ligand / immunology
  • Animals
  • Antigens, Neoplasm / administration & dosage*
  • Antigens, Neoplasm / genetics
  • Antigens, Neoplasm / immunology
  • Cell Line, Tumor / transplantation
  • Disease Models, Animal
  • Female
  • Fibronectins / genetics
  • Fibronectins / immunology
  • Humans
  • Mice
  • Neoplasms / drug therapy*
  • Neoplasms / immunology
  • Protein Domains / genetics
  • Protein Domains / immunology
  • Protein Engineering
  • Recombinant Fusion Proteins / administration & dosage*
  • Recombinant Fusion Proteins / genetics
  • Recombinant Fusion Proteins / immunology

Substances

  • 4-1BB Ligand
  • Antigens, Neoplasm
  • Fibronectins
  • Recombinant Fusion Proteins
  • Tnfsf9 protein, mouse