Clinical and Prognostic Features of Essential Thrombocythemia: Comparison of 2001 WHO Versus 2008/2016 WHO Criteria in a Large Single-center Cohort

Clin Lymphoma Myeloma Leuk. 2021 Apr;21(4):e328-e333. doi: 10.1016/j.clml.2020.11.003. Epub 2020 Nov 6.

Abstract

Background: According to 2008/2016 classification of the World Health Organization (WHO), a platelet (PLT) count ≥ 450 × 109/L, reduced from the previously published WHO 2001 indicated level ≥ 600 × 109/L, was considered the new PLT threshold for the diagnosis of essential thrombocythemia (ET).

Patients and methods: To validate this important diagnostic change in a setting of current clinical practice, we retrospectively analyzed clinical and hematologic features at diagnosis and during follow-up of 162 patients with ET, diagnosed in our center from January 2008 to December 2017. We subdivided patients according to PLT value at baseline into Group A (PLT ≥ 600 × 109/L) (124 patients; 76.5%) and Group B (PLT ≥ 450 × 109/L < 600 × 109/L) (38 patients; 23.5%).

Results: Among clinical features, only the median value of leukocytes (P < .001) was significantly higher in Group A. Cytostatic treatment was administered in 103 patients, with a significantly higher rate in patients of group A (P < .001). After a median follow-up of 42.4 months (interquartile range, 22.1-70.6 months), 8 thrombotic events were recorded in the entire cohort, without differences between the 2 groups (P = .336). The 5-year overall survival (OS) of the entire cohort was 96.9% (95% confidence interval, 92.6%-100%), without differences between the 2 groups (P = .255).

Conclusions: Our data indicate a substantial homogeneity among patients with ET regardless of the PLT count at diagnosis, thus confirming the usefulness of the 2008/2016 WHO diagnostic criteria.

Keywords: Diagnostic threshold; Platelets; Real-life assessment; Thrombosis; WHO classification.

Publication types

  • Comparative Study

MeSH terms

  • Aged
  • Cytostatic Agents / administration & dosage*
  • Feasibility Studies
  • Female
  • Follow-Up Studies
  • Humans
  • Leukocyte Count
  • Male
  • Middle Aged
  • Platelet Count / standards*
  • Prognosis
  • Reference Values
  • Retrospective Studies
  • Risk Factors
  • Thrombocythemia, Essential / blood
  • Thrombocythemia, Essential / complications
  • Thrombocythemia, Essential / diagnosis*
  • Thrombocythemia, Essential / drug therapy
  • Thrombosis / blood
  • Thrombosis / epidemiology*
  • Thrombosis / etiology
  • Thrombosis / prevention & control
  • World Health Organization

Substances

  • Cytostatic Agents