Aquaporin-4-antibody-positive Neuromyelitis Optica Spectrum Disorder in a Patient with Charcot-Marie-Tooth Disease Type 1A

Intern Med. 2021 May 15;60(10):1611-1614. doi: 10.2169/internalmedicine.6153-20. Epub 2020 Dec 22.

Abstract

Charcot-Marie-Tooth disease type 1A (CMT1A) is a hereditary peripheral neuropathy, and its involvement in the central nervous system (CNS) is very rare. We herein report a 51-year-old woman with CMT1A who suffered from recurrent optic neuritis and myelopathy. Under the diagnosis of anti-aquaporin-4 (anti-AQP4) antibody positive neuromyelitis optica spectrum disorder (NMOSD), we treated her successfully with corticosteroids. This is the first report of CMT1A complicated with anti-AQP4-positive NMOSD. Although the coexistence of the two disorders may simply be a coincidence, we speculated that immune cross-reaction between overexpressed peripheral myelin protein 22 and CNS myelin may have caused concomitant CMT1A and NMOSD.

Keywords: Charcot-Marie-Tooth disease type 1A; anti-aquaporin-4 antibody; neuromyelitis optica spectrum disorder; optic neuritis.

Publication types

  • Case Reports

MeSH terms

  • Aquaporin 4
  • Autoantibodies
  • Charcot-Marie-Tooth Disease* / complications
  • Charcot-Marie-Tooth Disease* / diagnosis
  • Charcot-Marie-Tooth Disease* / genetics
  • Female
  • Humans
  • Middle Aged
  • Neuromyelitis Optica* / complications
  • Neuromyelitis Optica* / diagnosis
  • Optic Neuritis*

Substances

  • Aquaporin 4
  • Autoantibodies