A Fbxo48 inhibitor prevents pAMPKα degradation and ameliorates insulin resistance

Nat Chem Biol. 2021 Mar;17(3):298-306. doi: 10.1038/s41589-020-00723-0. Epub 2021 Jan 25.

Abstract

The adenosine monophosphate (AMP)-activated protein kinase (Ampk) is a central regulator of metabolic pathways, and increasing Ampk activity has been considered to be an attractive therapeutic target. Here, we have identified an orphan ubiquitin E3 ligase subunit protein, Fbxo48, that targets the active, phosphorylated Ampkα (pAmpkα) for polyubiquitylation and proteasomal degradation. We have generated a novel Fbxo48 inhibitory compound, BC1618, whose potency in stimulating Ampk-dependent signaling greatly exceeds 5-aminoimidazole-4-carboxamide-1-β-ribofuranoside (AICAR) or metformin. This compound increases the biological activity of Ampk not by stimulating the activation of Ampk, but rather by preventing activated pAmpkα from Fbxo48-mediated degradation. We demonstrate that, consistent with augmenting Ampk activity, BC1618 promotes mitochondrial fission, facilitates autophagy and improves hepatic insulin sensitivity in high-fat-diet-induced obese mice. Hence, we provide a unique bioactive compound that inhibits pAmpkα disposal. Together, these results define a new pathway regulating Ampk biological activity and demonstrate the potential utility of modulating this pathway for therapeutic benefit.

Publication types

  • Research Support, N.I.H., Extramural
  • Research Support, Non-U.S. Gov't
  • Research Support, U.S. Gov't, Non-P.H.S.

MeSH terms

  • AMP-Activated Protein Kinases / genetics*
  • AMP-Activated Protein Kinases / metabolism
  • Aminoimidazole Carboxamide / analogs & derivatives
  • Aminoimidazole Carboxamide / pharmacology
  • Animals
  • Cell Line, Transformed
  • Diet, High-Fat
  • Epithelial Cells / cytology
  • Epithelial Cells / drug effects
  • Epithelial Cells / metabolism
  • F-Box Proteins
  • Humans
  • Hypoglycemic Agents / chemical synthesis
  • Hypoglycemic Agents / pharmacology*
  • Insulin Resistance
  • Metformin / pharmacology
  • Mice
  • Mice, Inbred C57BL
  • Mice, Obese
  • Mitochondrial Dynamics / drug effects
  • Obesity / drug therapy*
  • Obesity / etiology
  • Obesity / genetics
  • Obesity / metabolism
  • Phosphorylation
  • Polyubiquitin / genetics
  • Polyubiquitin / metabolism
  • Proteasome Endopeptidase Complex / drug effects*
  • Proteasome Endopeptidase Complex / metabolism
  • Protein Processing, Post-Translational / drug effects*
  • Protein Stability / drug effects
  • Proteolysis / drug effects
  • Ribonucleotides / pharmacology
  • Ubiquitin-Protein Ligases / antagonists & inhibitors
  • Ubiquitin-Protein Ligases / genetics*
  • Ubiquitin-Protein Ligases / metabolism
  • Ubiquitination

Substances

  • F-Box Proteins
  • Hypoglycemic Agents
  • Ribonucleotides
  • Polyubiquitin
  • Aminoimidazole Carboxamide
  • Metformin
  • FBXO48 protein, human
  • Ubiquitin-Protein Ligases
  • AMP-Activated Protein Kinases
  • PRKAA1 protein, human
  • Proteasome Endopeptidase Complex
  • AICA ribonucleotide