Loss of CTNNB1 exon 3 in sclerosing angiomatoid nodular transformation of the spleen

Virchows Arch. 2021 Oct;479(4):747-754. doi: 10.1007/s00428-021-03064-y. Epub 2021 Mar 1.

Abstract

Sclerosing angiomatoid nodular transformation (SANT) is a rare vascular lesion of the spleen. Although several hypotheses have been suggested, the etiopathogenesis of SANT remains unknown. It is also unclear whether SANT is a reactive or a neoplastic lesion. Since CTNNB1 (β-catenin gene) exon 3 mutations were frequently detected in some rare fibrovascular lesions, we aimed to investigate the presence of oncogenic CTNNB1 mutations in SANT cases. For this purpose, 7 cases of SANT with typical histopathological features were retrieved. First, the presence of CTNNB1 exon 3 alterations was examined with a recently described immunohistochemistry-based method. Then, the findings were confirmed with polymerase chain reaction (PCR), reverse transcription PCR (RT-PCR), and Sanger sequencing. In all cases, immunochemistry of β-catenin gave a staining pattern that was suggestive of exon 3 alteration; however, no missense mutations were found in any case at the CTNNB1 exon 3 hotspot region. Subsequently, we screened for large interstitial deletions of CTNNB1 exon 3 which revealed short PCR products in three cases. Sequencing confirmed that these cases had large interstitial deletions, resulting in loss of the entire exon 3 of CTNNB1. In the remaining four cases, loss of exon 3 was documented at the cDNA level, although genomic deletion was not identified. These results demonstrate that loss of CTNNB1 exon 3 and stabilization of β-catenin with activation of Wnt signaling pathway might have a significant role in the pathogenesis of SANT. Through this study, we provided important evidence for the neoplastic nature and pathogenesis of this disorder.

Keywords: CTNNB1; Exon 3; Sclerosing angiomatoid nodular transformation of spleen; Wnt; β-Catenin.

MeSH terms

  • Adult
  • Aged
  • Exons / genetics
  • Female
  • Histiocytoma, Benign Fibrous / genetics
  • Histiocytoma, Benign Fibrous / pathology*
  • Humans
  • Immunohistochemistry / methods
  • Male
  • Middle Aged
  • Oncogenes
  • Retrospective Studies
  • Sclerosing Solutions
  • Spleen / pathology*
  • Splenic Neoplasms / pathology
  • Wnt Signaling Pathway
  • beta Catenin / genetics*
  • beta Catenin / metabolism
  • beta Catenin / physiology

Substances

  • CTNNB1 protein, human
  • Sclerosing Solutions
  • beta Catenin