4-Hydroxybutyric aciduria in a patient without ataxia or convulsions

Eur J Pediatr. 1988 Jun;147(5):529-31. doi: 10.1007/BF00441983.

Abstract

A child presenting with mild psychomotor retardation, hypotonia, microcephaly and hyperkinesis is described. Urinary organic acid analysis by combined gas chromatography-mass spectrometry revealed 4-hydroxybutyric aciduria. Succinic semialdehyde dehydrogenase activity in extracts of white cells derived from the patient was less than 10% of control values.

Publication types

  • Case Reports
  • Research Support, Non-U.S. Gov't
  • Research Support, U.S. Gov't, P.H.S.

MeSH terms

  • Ataxia / etiology
  • Child
  • Female
  • Humans
  • Hydroxybutyrates / urine*
  • Hyperkinesis / etiology
  • Intellectual Disability / etiology
  • Muscle Hypotonia / etiology
  • Seizures / etiology
  • Sodium Oxybate / urine*

Substances

  • Hydroxybutyrates
  • Sodium Oxybate