Nusinersen improved respiratory function in spinal muscular atrophy type 2

Pediatr Int. 2021 Aug;63(8):973-974. doi: 10.1111/ped.14510. Epub 2021 Jul 10.

Authors

Ryuta Tanaka^{1

2}, Fujiko Fukushima¹, Keiichi Motoyama¹, Chie Kobayashi^{1

2}, Isho Izumi¹

Affiliations

¹ Department of Pediatrics, Ibaraki Children's Hospital, Mito-shi, Ibaraki-ken, Japan.
² Ibaraki Pediatric Education and Training Station, University of Tsukuba, Mito-shi, Ibaraki-ken, Japan.

PMID: 34245199
DOI: 10.1111/ped.14510

No abstract available

Keywords: Nusinersen; noninvasive ventilation; respiratory function tests; respiratory insufficiency; spinal muscular atrophies of childhood.

MeSH terms

Humans
Infant
Injections, Spinal
Muscular Atrophy, Spinal* / drug therapy
Oligonucleotides / therapeutic use
Respiration, Artificial
Spinal Muscular Atrophies of Childhood* / drug therapy

Substances

Oligonucleotides
nusinersen