Discovery of a dual Ras and ARF6 inhibitor from a GPCR endocytosis screen

Nat Commun. 2021 Aug 3;12(1):4688. doi: 10.1038/s41467-021-24968-y.

Abstract

Internalization and intracellular trafficking of G protein-coupled receptors (GPCRs) play pivotal roles in cell responsiveness. Dysregulation in receptor trafficking can lead to aberrant signaling and cell behavior. Here, using an endosomal BRET-based assay in a high-throughput screen with the prototypical GPCR angiotensin II type 1 receptor (AT1R), we sought to identify receptor trafficking inhibitors from a library of ~115,000 small molecules. We identified a novel dual Ras and ARF6 inhibitor, which we named Rasarfin, that blocks agonist-mediated internalization of AT1R and other GPCRs. Rasarfin also potently inhibits agonist-induced ERK1/2 signaling by GPCRs, and MAPK and Akt signaling by EGFR, as well as prevents cancer cell proliferation. In silico modeling and in vitro studies reveal a unique binding modality of Rasarfin within the SOS-binding domain of Ras. Our findings unveil a class of dual small G protein inhibitors for receptor trafficking and signaling, useful for the inhibition of oncogenic cellular responses.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • ADP-Ribosylation Factor 6
  • ADP-Ribosylation Factors / antagonists & inhibitors*
  • ADP-Ribosylation Factors / metabolism
  • Binding Sites
  • Bioluminescence Resonance Energy Transfer Techniques
  • Cell Line, Tumor
  • Cell Proliferation / drug effects
  • Drug Discovery
  • Endocytosis / drug effects*
  • Enzyme Inhibitors / chemistry
  • Enzyme Inhibitors / metabolism
  • Enzyme Inhibitors / pharmacology*
  • HEK293 Cells
  • Humans
  • Molecular Dynamics Simulation
  • Receptor Protein-Tyrosine Kinases / metabolism
  • Receptors, G-Protein-Coupled / metabolism*
  • Signal Transduction / drug effects
  • ras Proteins / antagonists & inhibitors*
  • ras Proteins / chemistry
  • ras Proteins / metabolism

Substances

  • ADP-Ribosylation Factor 6
  • Enzyme Inhibitors
  • Receptors, G-Protein-Coupled
  • Receptor Protein-Tyrosine Kinases
  • ADP-Ribosylation Factors
  • ARF6 protein, human
  • ras Proteins