Case study of betibeglogene autotemcel gene therapy in an adult Greek patient with transfusion-dependent β-thalassaemia of a severe genotype

Br J Haematol. 2022 Mar;196(6):1401-1404. doi: 10.1111/bjh.17965. Epub 2021 Dec 27.

Affiliations

¹ Gene and Cell Therapy Center of the Hematology Department/Hematopoietic Cell Transplantation Unit, G. Papanikolaou Hospital, Thessaloniki, Greece.
² Thalassaemia Unit, AHEPA University Hospital, Thessaloniki, Greece.

PMID: 34957544
DOI: 10.1111/bjh.17965

No abstract available

Keywords: gene therapy; haemoglobinopathies; thalassaemia.

Publication types

Letter
Research Support, Non-U.S. Gov't

MeSH terms

Adult
Genetic Therapy
Genotype
Greece
Humans
Hydroxyurea
beta-Thalassemia* / genetics
beta-Thalassemia* / therapy

Substances

Hydroxyurea