Child with a mild CHIME syndrome phenotype and carrying a novel p.(Asp52Asn) PIGL pathogenic variant in association with the previously reported p.(Leu167Pro) variant: A case report

Pediatr Dermatol. 2022 May;39(3):434-437. doi: 10.1111/pde.14969. Epub 2022 Mar 8.

Abstract

Coloboma, congenital heart disease, ichthyosiform dermatosis, mental retardation, and ear anomalies (CHIME) syndrome is a very rare autosomal recessive neuroectodermal disorder related to PIGL gene mutations. Here, we report a patient who showed an initial delay in psychomotor development and skin abnormalities consistent with CHIME syndrome but with atypical clinical features and laboratory findings. In line with our clinical suspicion, the c.500T>C, p.(Leu167Pro) variant (found in all the previously described cases of CHIME syndrome) was found on the paternal allele. A novel "likely pathogenic" PIGL missense variant (c.154G>A, p.(Asp52Asn)) was detected on the maternal allele. This case provides new insights into the clinical spectrum of CHIME syndrome and highlights the potential for phenotypic/genotypic variations.

Keywords: PIGL; CHIME syndrome; case report; neuroectodermal disorder.

Publication types

  • Case Reports

MeSH terms

  • Coloboma*
  • Hearing Loss, Conductive
  • Heart Defects, Congenital* / genetics
  • Humans
  • Ichthyosis
  • Intellectual Disability* / genetics
  • N-Acetylglucosaminyltransferases / genetics
  • Neurocutaneous Syndromes
  • Phenotype
  • Syndrome

Substances

  • N-Acetylglucosaminyltransferases
  • PIGL protein, human

Supplementary concepts

  • Zunich neuroectodermal syndrome