Sequential Treatment With Trifluridine/Tipiracil and Regorafenib in Refractory Metastatic Colorectal Cancer Patients: An AGEO Prospective "Real-World Study"

Clin Colorectal Cancer. 2022 Jun;21(2):132-140. doi: 10.1016/j.clcc.2021.12.003. Epub 2022 Feb 14.

Abstract

Introduction: Regorafenib (R) and trifluridine/tipiracil (FTD/TPI) are of proven efficacy in metastatic colorectal cancer (mCRC) patient's refractory to standard therapies. However, it remains unclear which drug should be administered first.

Patients and methods: This French observational study was prospectively conducted in 11 centers between June 2017 and September 2019. All consecutive patients with chemorefractory mCRC and receiving FTD/TPI and/or R were eligible. The aim was to evaluate the efficacy and tolerability of FTD/TPI and/or R in real-world setting with adjusted analysis.

Results: A total of 237 mCRC patients (25% R and 75% FTD/TPI) were enrolled. As compared to R, FTD/TPI patients were significantly older and with more metastatic sites. Median OS and PFS were respectively 6.2 and 2.4 months in the FTD/TPI and 6.6 and 2.1 months in the R group. After matching 46 paired patients according to a propensity score, a trend to a longer OS (P = .58), and a significantly longer PFS (P = .048) were observed in the FTD/TPI group. In the 24% of patients receiving the R/T or T/R sequence, median OS from first treatment was similar. Tolerability profiles were similar to published data and dose reductions were more frequent in the R group.

Conclusion: Efficacy and safety results in this real-world prospective study are in line with phase III trials. In a matched population, PFS was significantly longer in the FTD/TPI group. Despite a limited number of patients, clinical outcomes seemed similar in patients treated with the T/R or R/T sequence.

Keywords: metastatic colorectal cancer; regorafenib; trifluridine/tipiracil.

Publication types

  • Observational Study
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Antineoplastic Combined Chemotherapy Protocols / adverse effects
  • Colonic Neoplasms* / drug therapy
  • Colorectal Neoplasms* / drug therapy
  • Colorectal Neoplasms* / pathology
  • Drug Combinations
  • Frontotemporal Dementia* / chemically induced
  • Frontotemporal Dementia* / drug therapy
  • Humans
  • Phenylurea Compounds
  • Prospective Studies
  • Pyridines
  • Pyrrolidines
  • Rectal Neoplasms* / drug therapy
  • Thymine
  • Trifluridine / adverse effects
  • Uracil / adverse effects

Substances

  • Drug Combinations
  • Phenylurea Compounds
  • Pyridines
  • Pyrrolidines
  • regorafenib
  • Uracil
  • tipiracil
  • Thymine
  • Trifluridine