Selection and characterization of DNA aptamers inhibiting a druggable target of osteoarthritis, ADAMTS-5

Biochimie. 2022 Oct:201:168-176. doi: 10.1016/j.biochi.2022.06.001. Epub 2022 Jun 11.

Abstract

There is a critical need for the development of more potent inhibitors for osteoarthritis (OA) therapy given the poor life quality of arthritis patients. Aggrecanase ADAMTS-5 (a disintegrin and metalloproteinase with thrombospondin motifs 5) is an established drug target identified for osteoarthritis. In this study, we evolved and characterized two new DNA aptamer inhibitors of ADAMTS-5, namely apt21 and apt25. The aptamers exhibited nanomolar binding affinity and high specificity against ADAMTS-5. KD values of apt21 and apt25 were determined by the Enzyme-linked Oligonucleotide Assay (ELONA) at 1.54 ± 0.16 nM and 1.79 ± 0.08 nM, respectively. Circular Dichroism (CD) analysis demonstrated that both aptamers formed monovalent cation dependent G-quadruplex structures. Calcium ions did not affect the binding of the aptamers to ADAMTS-5. The inhibitory effects of apt21 and apt25 on ADAMTS-5 were evaluated by the Förster Resonance Energy Transfer (FRET) assay, in which IC50 values of apt21 and apt25 were estimated at 52.76 ± 6.70 μM and 61.14 ± 9.67 μM, respectively. These two aptamers are the first DNA G-quadruplex aptamers demonstrated to inhibit ADAMTS-5 and could have value for OA therapy.

Keywords: ADAMTS-5; DNA aptamers; G-quadruplex; Inhibitor; Osteoarthritis.

MeSH terms

  • ADAMTS4 Protein / chemistry
  • ADAMTS4 Protein / genetics
  • ADAMTS4 Protein / metabolism
  • ADAMTS5 Protein / genetics
  • ADAMTS5 Protein / metabolism
  • Aptamers, Nucleotide* / pharmacology
  • Calcium
  • Cations, Monovalent
  • DNA
  • Disintegrins
  • Humans
  • Osteoarthritis* / drug therapy
  • Thrombospondins

Substances

  • Aptamers, Nucleotide
  • Cations, Monovalent
  • Disintegrins
  • Thrombospondins
  • DNA
  • ADAMTS5 Protein
  • ADAMTS4 Protein
  • Calcium