Targeting NAAA counters dopamine neuron loss and symptom progression in mouse models of parkinsonism

Pharmacol Res. 2022 Aug:182:106338. doi: 10.1016/j.phrs.2022.106338. Epub 2022 Jun 30.

Abstract

The lysosomal cysteine hydrolase N-acylethanolamine acid amidase (NAAA) deactivates palmitoylethanolamide (PEA), a lipid-derived PPAR-α agonist that is critically involved in the control of pain and inflammation. In this study, we asked whether NAAA-regulated PEA signaling might contribute to dopamine neuron degeneration and parkinsonism induced by the mitochondrial neurotoxins, 6-hydroxydopamine (6-OHDA) and 1-methyl-4-phenyl-1,2,3,6-tetrahydropyridine (MPTP). In vitro experiments showed that 6-OHDA and MPTP enhanced NAAA expression and lowered PEA content in human SH-SY5Y cells. A similar effect was observed in mouse midbrain dopamine neurons following intra-striatal 6-OHDA injection. Importantly, deletion of the Naaa gene or pharmacological inhibition of NAAA activity substantially attenuated both dopamine neuron death and parkinsonian symptoms in mice treated with 6-OHDA or MPTP. Moreover, NAAA expression was elevated in postmortem brain cortex and premortem blood-derived exosomes from persons with Parkinson's disease compared to age-matched controls. The results identify NAAA-regulated PEA signaling as a molecular control point for dopaminergic neuron survival and a potential target for neuroprotective intervention.

Keywords: N-Acylethanolamine Acid Amidase; Neurodegeneration; Neuroinflammation; Palmitoylethanolamide; Parkinson's disease.

Publication types

  • Research Support, N.I.H., Extramural
  • Research Support, Non-U.S. Gov't

MeSH terms

  • 1-Methyl-4-phenyl-1,2,3,6-tetrahydropyridine
  • Amidohydrolases
  • Animals
  • Disease Models, Animal
  • Dopamine
  • Dopaminergic Neurons / metabolism
  • Enzyme Inhibitors / pharmacology
  • Humans
  • Mice
  • Nerve Degeneration / drug therapy
  • Neuroblastoma* / drug therapy
  • Oxidopamine
  • Parkinsonian Disorders* / chemically induced
  • Parkinsonian Disorders* / drug therapy

Substances

  • Enzyme Inhibitors
  • Oxidopamine
  • 1-Methyl-4-phenyl-1,2,3,6-tetrahydropyridine
  • Amidohydrolases
  • NAAA protein, human
  • Dopamine