Correction to: Sharing is caring: a call for a new era of rare disease research and development

Affiliations

• ¹ Gene Therapy Program, Department of Medicine, Perelman School of Medicine, University of Pennsylvania, Philadelphia, PA, 19104, USA. [email protected].
• ² Neurogene Inc., New York, NY, USA.
• ³ Department of Medicine, Orphan Disease Center, Perelman School of Medicine, University of Pennsylvania, Philadelphia, PA, 19104, USA.
• ⁴ Translational Medicine & Human Genetics, Perelman School of Medicine, University of Pennsylvania, Philadelphia, PA, 19104, USA.
• ⁵ Department of Medicine, Orphan Disease Center, Perelman School of Medicine, University of Pennsylvania, Philadelphia, PA, 19104, USA. [email protected].
• ⁶ Departments of Neurology and Pediatrics, Children's Hospital of Philadelphia, Perelman School of Medicine, University of Pennsylvania, Philadelphia, PA, 19104, USA. [email protected].
• ⁷ Division of Neurology, Children's Hospital of Philadelphia, Philadelphia, PA, 19104, USA. [email protected].
• ⁸ Amicus Therapeutics, Philadelphia, PA, 19104, USA. [email protected].