Access to new drugs in paediatric oncology: can we learn from the ongoing ONC201 saga?

Affiliations

• ¹ Department of Pediatric Oncology, La Timone University Hospital of Marseille, APHM, Marseille 13005, France; SMARTc Unit, CRCM Inserm 1068- CNRS UMR 7258 Aix-Marseille University, Marseille, France. Electronic address: [email protected].
• ² The Anticancer Fund, Brussels, Belgium.
• ³ Division of Neuro-oncology, Department of Pediatric Hematology-Oncology, Hospital for Sick Children, Toronto, ON, Canada.
• ⁴ University of Nottingham, Nottingham, UK.
• ⁵ Cancer Signalling Research Group, School of Biomedical Sciences and Pharmacy, College of Health, Medicine & Wellbeing, University of Newcastle, Callaghan, NSW, Australia; Precision Medicine Research Program, Hunter Medical Research Institute, New Lambton Heights, NSW, Australia.