Randomized phase II clinical trial of ruxolitinib plus simvastatin in COVID19 clinical outcome and cytokine evolution

Front Immunol. 2023 Apr 18:14:1156603. doi: 10.3389/fimmu.2023.1156603. eCollection 2023.

Abstract

Background: Managing the inflammatory response to SARS-Cov-2 could prevent respiratory insufficiency. Cytokine profiles could identify cases at risk of severe disease.

Methods: We designed a randomized phase II clinical trial to determine whether the combination of ruxolitinib (5 mg twice a day for 7 days followed by 10 mg BID for 7 days) plus simvastatin (40 mg once a day for 14 days), could reduce the incidence of respiratory insufficiency in COVID-19. 48 cytokines were correlated with clinical outcome.

Participants: Patients admitted due to COVID-19 infection with mild disease.

Results: Up to 92 were included. Mean age was 64 ± 17, and 28 (30%) were female. 11 (22%) patients in the control arm and 6 (12%) in the experimental arm reached an OSCI grade of 5 or higher (p = 0.29). Unsupervised analysis of cytokines detected two clusters (CL-1 and CL-2). CL-1 presented a higher risk of clinical deterioration vs CL-2 (13 [33%] vs 2 [6%] cases, p = 0.009) and death (5 [11%] vs 0 cases, p = 0.059). Supervised Machine Learning (ML) analysis led to a model that predicted patient deterioration 48h before occurrence with a 85% accuracy.

Conclusions: Ruxolitinib plus simvastatin did not impact the outcome of COVID-19. Cytokine profiling identified patients at risk of severe COVID-19 and predicted clinical deterioration.

Trial registration: https://clinicaltrials.gov/, identifier NCT04348695.

Keywords: COVID19; SARS-Cov-2; clinical trial; cytokine storm; ruxolitinib; simvastatin.

Publication types

  • Randomized Controlled Trial
  • Clinical Trial, Phase II
  • Research Support, Non-U.S. Gov't

MeSH terms

  • COVID-19*
  • Clinical Deterioration*
  • Female
  • Humans
  • Male
  • Respiratory Insufficiency*
  • SARS-CoV-2
  • Treatment Outcome

Substances

  • ruxolitinib

Associated data

  • ClinicalTrials.gov/NCT04348695

Grants and funding

The Ruxo-Sim trial has been funded by Novartis INC through an unrestricted grant. Novartis also provided ruxolitinib. Novartis did not play any role in study design, analysis or communication. Cytokine analysis has been mainly funded by the Instituto de Salud Carlos III through Fondos COVID-19 (COV20/00211). Additionally, the project has received funding from the European Research Council (ERC) under the European Union's Horizon 2020 research and innovation programme (grant agreement No 851255). MZ acknowledges the María de Maeztu project CEX2021-001164-M funded by the MCIN/AEI/10.13039/501100011033. PB received funds from Instituto de Salud Carlos III (PI20/00002) cofinanced by Fondos Feder, and Gobierno de Navarra Proyecto LINTERNA Ref.: 0011-1411-2020-000075.