Current and Future Perspective in Hematopoietic Stem Progenitor Cell-gene Therapy for Inborn Errors of Metabolism

Hemasphere. 2023 Sep 12;7(10):e953. doi: 10.1097/HS9.0000000000000953. eCollection 2023 Oct.

Authors

Francesca Tucci^{1

2}, Giulia Consiglieri^{1

2

3}, Matilde Cossutta^{1

4}, Maria Ester Bernardo^{1

2

5}

Affiliations

¹ Pediatric Immunohematology and Bone Marrow Transplantation, IRCCS San Raffaele Scientific Institute, Milan, Italy.
² San Raffaele Telethon Institute for Gene Therapy (SR-TIGET), Milan, Italy.
³ Department of Biomedicine and Prevention, University of Rome Tor Vergata, Italy.
⁴ University of Rome Tor Vergata, Italy.
⁵ "Vita-Salute" San Raffaele University, Milan, Italy.

No abstract available

Publication types

Editorial