Optogenetic induction of alpha-synuclein aggregation in human dopaminergic neurons to model Parkinson's disease pathology

STAR Protoc. 2023 Dec 15;4(4):102609. doi: 10.1016/j.xpro.2023.102609. Epub 2023 Sep 23.

Abstract

Alpha-synuclein (α-syn) aggregation is a principal factor in Parkinson's disease (PD) onset. Here, we present a protocol for optogenetic induction of α-syn aggregation in human midbrain dopaminergic (mDA) neurons, facilitating a detailed PD pathology study. We describe steps for nucleofection of the opto-α-syn construct, single colony selection and validation, alongside mDA neuron differentiation and rapid induction of toxic α-syn aggregates via blue light. This establishes a potent human induced pluripotent-stem-cell-based platform for PD drug testing and validation. For complete details on the use and execution of this protocol, please refer to Kim et al. (2023).1.

Keywords: Cell Differentiation; Organoids; Stem Cells.

MeSH terms

  • Dopaminergic Neurons / metabolism
  • Humans
  • Mesencephalon / metabolism
  • Optogenetics
  • Parkinson Disease* / genetics
  • Parkinson Disease* / pathology
  • alpha-Synuclein / genetics
  • alpha-Synuclein / metabolism

Substances

  • alpha-Synuclein