Genome-wide enhancer-gene regulatory maps link causal variants to target genes underlying human cancer risk

Nat Commun. 2023 Sep 25;14(1):5958. doi: 10.1038/s41467-023-41690-z.

Abstract

Genome-wide association studies have identified numerous variants associated with human complex traits, most of which reside in the non-coding regions, but biological mechanisms remain unclear. However, assigning function to the non-coding elements is still challenging. Here we apply Activity-by-Contact (ABC) model to evaluate enhancer-gene regulation effect by integrating multi-omics data and identified 544,849 connections across 20 cancer types. ABC model outperforms previous approaches in linking regulatory variants to target genes. Furthermore, we identify over 30,000 enhancer-gene connections in colorectal cancer (CRC) tissues. By integrating large-scale population cohorts (23,813 cases and 29,973 controls) and multipronged functional assays, we demonstrate an ABC regulatory variant rs4810856 associated with CRC risk (Odds Ratio = 1.11, 95%CI = 1.05-1.16, P = 4.02 × 10-5) by acting as an allele-specific enhancer to distally facilitate PREX1, CSE1L and STAU1 expression, which synergistically activate p-AKT signaling. Our study provides comprehensive regulation maps and illuminates a single variant regulating multiple genes, providing insights into cancer etiology.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Alleles
  • Chromosome Mapping
  • Cytoskeletal Proteins / genetics
  • Enhancer Elements, Genetic / genetics
  • Gene Expression Regulation
  • Genetic Predisposition to Disease
  • Genome-Wide Association Study*
  • Humans
  • Neoplasms* / genetics
  • Polymorphism, Single Nucleotide
  • RNA-Binding Proteins / genetics
  • Regulatory Sequences, Nucleic Acid

Substances

  • STAU1 protein, human
  • Cytoskeletal Proteins
  • RNA-Binding Proteins