Highly efficient biallelic correction of homozygous COL7A1 mutation using ABE8e adenine base editor

Affiliations

• ¹ St John's Institute of Dermatology, King's College London, London, UK.
• ² Hirszfeld Institute of Immunology and Experimental Therapy, Polish Academy of Sciences, Wroclaw, Poland.
• ³ Merkin Institute of Transformative Technologies in Healthcare, Broad Institute of Harvard and MIT, Cambridge, MA, USA.
• ⁴ Department of Chemistry and Chemical Biology, Harvard University, Cambridge, MA, USA.
• ⁵ Howard Hughes Medical Institute, Harvard University, Cambridge, MA, USA.