Rescue of a lysosomal storage disorder caused by Grn loss of function with a brain penetrant progranulin biologic

Cell. 2024 Mar 14;187(6):1565-1566. doi: 10.1016/j.cell.2024.02.015.

Authors

Todd Logan, Matthew J Simon, Anil Rana, Gerald M Cherf, Ankita Srivastava, Sonnet S Davis, Ray Lieh Yoon Low, Chi-Lu Chiu, Meng Fang, Fen Huang, Akhil Bhalla, Ceyda Llapashtica, Rachel Prorok, Michelle E Pizzo, Meredith E K Calvert, Elizabeth W Sun, Jennifer Hsiao-Nakamoto, Yashas Rajendra, Katrina W Lexa, Devendra B Srivastava, Bettina van Lengerich, Junhua Wang, Yaneth Robles-Colmenares, Do Jin Kim, Joseph Duque, Melina Lenser, Timothy K Earr, Hoang Nguyen, Roni Chau, Buyankhishig Tsogtbaatar, Ritesh Ravi, Lukas L Skuja, Hilda Solanoy, Howard J Rosen, Bradley F Boeve, Adam L Boxer, Hilary W Heuer, Mark S Dennis, Mihalis S Kariolis, Kathryn M Monroe, Laralynne Przybyla, Pascal E Sanchez, Rene Meisner, Dolores Diaz, Kirk R Henne, Ryan J Watts, Anastasia G Henry, Kannan Gunasekaran, Giuseppe Astarita, Jung H Suh, Joseph W Lewcock, Sarah L DeVos, Gilbert Di Paolo

PMID: 38490183
PMCID: PMC11089899 (available on 2025-03-14)
DOI: 10.1016/j.cell.2024.02.015

No abstract available

Publication types

Published Erratum

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