A 10-year follow-up of high-dose ambroxol treatment combined with enzyme replacement therapy for neuropathic Gaucher disease

Am J Hematol. 2024 Jul;99(7):1396-1399. doi: 10.1002/ajh.27302. Epub 2024 Apr 1.

Abstract

High-dose ambroxol therapy combined with ERT in patients with neuropathic Gaucher disease.

Publication types

  • Letter
  • Case Reports
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Adult
  • Ambroxol* / administration & dosage
  • Ambroxol* / therapeutic use
  • Drug Therapy, Combination
  • Enzyme Replacement Therapy*
  • Female
  • Follow-Up Studies
  • Gaucher Disease* / drug therapy
  • Glucosylceramidase* / administration & dosage
  • Glucosylceramidase* / therapeutic use
  • Humans
  • Male
  • Middle Aged

Substances

  • Ambroxol
  • Glucosylceramidase