Genetic Assessment of Intraductal Papillary Mucinous Neoplasm for Predicting Concomitant Pancreatic Ductal Adenocarcinoma

Pancreas. 2024 Nov-Dec;53(10):e790-e795. doi: 10.1097/MPA.0000000000002373. Epub 2024 May 15.

Abstract

Objective: The role of Krüppel-like transcription factor 4 ( KLF4 ) mutations in IPMNs with concomitant pancreatic ductal adenocarcinoma (PDAC) remains unclear. This study clarified the rate and effect of KLF4 mutations in IPMN with concomitant PDAC.

Materials and methods: DNA was extracted from 65 formalin-fixed and paraffin-embedded samples from 52 patients including 13 IPMNs with concomitant PDAC and 39 IPMNs alone. A comprehensive screening using next-generation sequencing and then targeted sequencing for KLF4 , GNAS , and KRAS mutations were performed.

Results: In next-generation sequencing screening, KRAS mutations were observed in all samples except for one, GNAS mutation in 2 IPMNs with concomitant PDAC, and a KLF4 mutation in 1 IPMN with concomitant PDAC. Targeted sequence detected KLF4 mutations in 11 of the 52 IPMNs. Concomitant PDAC developed only in the nonintestinal, noninvasive, and branch-duct IPMNs, and KLF4 mutations were more frequent in this IPMN type than in the other type. For this IPMN type with KLF4 mutation, PDAC-prediction sensitivity, specificity, and accuracy were 63%, 82%, and 79%, respectively.

Conclusion: For selected IPMNs with nonintestinal, noninvasive, and branch-duct, genetic assessment might be helpful for predicting the possible development of concomitant PDAC, although a prospective validation study using a larger study population is needed.

MeSH terms

  • Adenocarcinoma, Mucinous / genetics
  • Adenocarcinoma, Mucinous / pathology
  • Adult
  • Aged
  • Aged, 80 and over
  • Carcinoma, Pancreatic Ductal* / genetics
  • Chromogranins / genetics
  • Female
  • GTP-Binding Protein alpha Subunits, Gs* / genetics
  • High-Throughput Nucleotide Sequencing / methods
  • Humans
  • Kruppel-Like Factor 4*
  • Kruppel-Like Transcription Factors* / genetics
  • Male
  • Middle Aged
  • Mutation*
  • Pancreatic Intraductal Neoplasms / genetics
  • Pancreatic Intraductal Neoplasms / pathology
  • Pancreatic Neoplasms* / genetics
  • Proto-Oncogene Proteins p21(ras) / genetics

Substances

  • Kruppel-Like Factor 4
  • KLF4 protein, human
  • Kruppel-Like Transcription Factors
  • GTP-Binding Protein alpha Subunits, Gs
  • GNAS protein, human
  • Proto-Oncogene Proteins p21(ras)
  • KRAS protein, human
  • Chromogranins