Pre-ANDA strategy and Human Factors activities to de-risk pharmaceutical companies ANDA submission of drug-device combination products: case study of a formative Comparative Use Human Factors study

Expert Opin Drug Deliv. 2024 May;21(5):767-778. doi: 10.1080/17425247.2024.2356678. Epub 2024 May 29.

Abstract

Background: This article presents a strategy that a Drug Delivery Device Developer (DDDD) has adopted to support Abbreviated New Drug Application (ANDA) submissions of drug-device combination products. As per the related FDA guidance, a threshold analysis should be compiled. If 'other differences' between the Reference Listed Drug (RLD) and the generic drug devices are identified, a Comparative Use Human Factors (CUHF) study may be requested.

Methods: The DDDD performed task analysis and physical comparison to assess the pen injector design differences. Then, a formative CUHF study with 25 participants simulating injections using both RLD and the generic pen injectors was conducted.

Results: After each participant completed four simulated injections, similar type and rates of use error between the RLD (0.70) and generic (0.68) pen injectors were observed.

Conclusion: DDDDs can support pharmaceutical companies in the ANDA submission strategy of their drug-device combination product by initiating comparative task analysis and physical comparison of the device as inputs for the threshold analysis. If 'other differences' are identified, a formative CUHF study can be performed. As shown in our case study, this approach can be leveraged to support the sample size calculation and non-inferiority margin determination for a CUHF study with the final combination product.

Keywords: ANDA; Comparative use human Factors; combination product; drug delivery system; generic; self-administration.

Publication types

  • Comparative Study

MeSH terms

  • Drug Approval
  • Drug Delivery Systems* / instrumentation
  • Drug Industry*
  • Drugs, Generic / administration & dosage
  • Equipment Design
  • Ergonomics
  • Humans
  • Injections
  • Male
  • Pharmaceutical Preparations / administration & dosage
  • Task Performance and Analysis
  • United States
  • United States Food and Drug Administration

Substances

  • Drugs, Generic
  • Pharmaceutical Preparations