Infliximab in paediatric inflammatory bowel disease: External evaluation of population pharmacokinetic models

Br J Clin Pharmacol. 2024 Sep;90(9):2200-2214. doi: 10.1111/bcp.16126. Epub 2024 Jun 6.

Abstract

Aims: Use of infliximab (IFX) has improved outcomes in children with inflammatory bowel disease (IBD). However, a proportion of patients does not respond to IFX or loses response over time. Population pharmacokinetic (PopPK) modelling is a promising approach for IFX dose optimization, but with the increasing number of PopPK models in literature, model evaluation is essential. The aims of this study are: (i) to validate the predictive performance of existing IFX PopPK models using a cohort of children with IBD; and (ii) to perform a Bayesian estimation of the most suitable model to predict the next IFX concentrations.

Methods: PubMed was searched for IFX PopPK models in children. Selected models were rebuilt and analysed using R. Model performance was assessed through goodness-of-fit-plots, residuals against time, prediction error and prediction-corrected visual predictive checks. The validation cohort consisted of 73 children with IBD who were treated with IFX in our centre between 2017 and 2023 (340 IFX measurements).

Results: We identified 9 PopPK models. Model bias for individual predicted values ranged from -9.29% to 8.01% compared to bias for population predicted values. The model by Vande Casteele et al. demonstrated superior performance (individual predicted bias 2.13, population predicted bias -6.11); upon Bayesian estimation, it predicted induction trough levels with median error of 12.95% but had a median error of -69% predicting maintenance concentrations.

Conclusion: The model by Vande Casteele et al. displayed superior performance in initial evaluations but had a high error in estimating next IFX levels and can only be used in practice to predict induction levels.

Keywords: IBD; PopPK; TDM; children; gastroenterology; infliximab; tumour necrosis factor‐α.

Publication types

  • Validation Study

MeSH terms

  • Adolescent
  • Bayes Theorem*
  • Child
  • Child, Preschool
  • Dose-Response Relationship, Drug
  • Female
  • Gastrointestinal Agents* / administration & dosage
  • Gastrointestinal Agents* / blood
  • Gastrointestinal Agents* / pharmacokinetics
  • Gastrointestinal Agents* / therapeutic use
  • Humans
  • Inflammatory Bowel Diseases / drug therapy
  • Infliximab* / administration & dosage
  • Infliximab* / blood
  • Infliximab* / pharmacokinetics
  • Infliximab* / therapeutic use
  • Male
  • Models, Biological*

Substances

  • Infliximab
  • Gastrointestinal Agents