Sensing and guiding cell-state transitions by using genetically encoded endoribonuclease-mediated microRNA sensors

Nat Biomed Eng. 2024 Dec;8(12):1730-1743. doi: 10.1038/s41551-024-01229-z. Epub 2024 Jul 9.

Abstract

Precisely sensing and guiding cell-state transitions via the conditional genetic activation of appropriate differentiation factors is challenging. Here we show that desired cell-state transitions can be guided via genetically encoded sensors, whereby endogenous cell-state-specific miRNAs regulate the translation of a constitutively transcribed endoribonuclease, which, in turn, controls the translation of a gene of interest. We used this approach to monitor several cell-state transitions, to enrich specific cell types and to automatically guide the multistep differentiation of human induced pluripotent stem cells towards a haematopoietic lineage via endothelial cells as an intermediate state. Such conditional activation of gene expression is durable and resistant to epigenetic silencing and could facilitate the monitoring of cell-state transitions in physiological and pathological conditions and eventually the 'rewiring' of cell-state transitions for applications in organoid-based disease modelling, cellular therapies and regenerative medicine.

MeSH terms

  • Biosensing Techniques / methods
  • Cell Differentiation* / genetics
  • Endoribonucleases* / genetics
  • Endoribonucleases* / metabolism
  • Endothelial Cells / metabolism
  • Humans
  • Induced Pluripotent Stem Cells* / metabolism
  • MicroRNAs* / genetics
  • MicroRNAs* / metabolism

Substances

  • MicroRNAs
  • Endoribonucleases